Malik, Punam
Gene and Cell Therapies for Beta-Globinopathies
1. Clinical Features of β-Thalassemia and Sickle Cell Disease
Patrick T. McGann, Alecia C. Nero, Russell E. Ware
2. Genetic Basis and Genetic Modifiers of β-Thalassemia and Sickle Cell Disease
Swee Lay Thein
3. Current Standards of Care and Long Term Outcomes for Thalassemia and Sickle Cell Disease
Satheesh Chonat, Charles T. Quinn
4. Allogeneic/Matched Related Transplantation for β-Thalassemia and Sickle Cell Anemia
Françoise Bernaudin, Corinne Pondarré, Claire Galambrun, Isabelle Thuret
5. Alternative Donor/Unrelated Donor Transplants for the β-Thalassemia and Sickle Cell Disease
Courtney D. Fitzhugh, Allistair Abraham, Matthew M. Hsieh
6. Gene Addition Strategies for β-Thalassemia and Sickle Cell Anemia
Alisa C. Dong, Stefano Rivella
7. Reactivation of Fetal Hemoglobin for Treating β-Thalassemia and Sickle Cell Disease
Shuaiying Cui, James Douglas Engel
8. Genome Editing for the β-Hemoglobinopathies
Matthew H. Porteus
9. Gene and Cell Therapy for β-Thalassemia and Sickle Cell Disease with Induced Pluripotent Stem Cells (iPSCs): The Next Frontier
Eirini P. Papapetrou
Keywords: Biomedicine, Gene Therapy, Cell Biology
- Editor
- Malik, Punam
- Tisdale, John
- Publisher
- Springer
- Publication year
- 2017
- Language
- en
- Edition
- 1
- Series
- Advances in Experimental Medicine and Biology
- Page amount
- 11 pages
- Category
- Medicine, Health Care, Mode
- Format
- Ebook
- eISBN (PDF)
- 9781493972999
- Printed ISBN
- 978-1-4939-7297-5