Muscle Gene Therapy

1. Animal Models for Inherited Muscle Diseases
Bruce F. Smith, Roberta Wrighten

2. In Utero Muscle Gene Transfer
Bhanu Munil Koppanati, Paula R. Clemens

3. Gene Therapy for the Respiratory Muscles
Gawiyou Danialou, Basil J. Petrof

4. Muscular Dystrophy Gene Therapy in Small Animal Models
Chunping Qiao, Xiao Xiao

5. Antisense-Mediated Exon Skipping for Duchenne Muscular Dystrophy
Annemieke Aartsma-Rus, Gert-Jan B Ommen

6. Systemic Treatment of Duchenne Muscular Dystrophy by Antisense Oligomer-Induced Exon Skipping
Qi Long Lu, Bo Wu

7. RNAi Therapy for Dominant Muscular Dystrophies and Other Myopathies
Lindsay M. Wallace, Sara E. Garwick, Scott Q. Harper

8. Combinatorial Gene Therapy Strategies for Treating Muscular Dystrophies
Catherine E. Winbanks, Paul Gregorevic

9. Duchenne Cardiomyopathy Gene Therapy
Jin-Hong Shin, Brian Bostick, Deborah M. Fine, Yongping Yue, Dongsheng Duan

10. Systemic Gene Delivery for Muscle Gene Therapy
Dilip Garikipati, Jeffrey S. Chamberlain

11. Modulating Immune Responses in Muscle Gene Therapy
Valder R. Arruda

12. Delivering Large Therapeutic Genes for Muscle Gene Therapy
Yi Lai, Yongping Yue, Brian Bostick, Dongsheng Duan

13. Muscle as a Metabolic Factory for Gene Therapy
Cathryn S. Mah, Christina A. Pacak, Barry J. Byrne

14. Muscle as a Target for Genetic Vaccine
Yan Zhi, Guangping Gao

15. Combining Stem Cells and Exon Skipping Strategy to Treat Muscular Dystrophy
Mirella Meregalli, Andrea Farini, Yvan Torrente

16. Gene Therapy Clinical Trials for Muscular Dystrophies
Dominic J. Wells

Keywords: Biomedicine, Human Genetics, Developmental Biology, Immunology, Virology